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Diagnosis Safe Moderate Evidence

Orphanet get gene diseases

by Harvard MIMS Lab (ToolUniverse)

Description

Get rare diseases associated with a gene from Orphanet. Accepts gene symbols (e.g., 'FBN1', 'BRCA1', 'HTT') or gene name keywords (e.g., 'fibrillin', 'huntingtin', 'dystrophin'). Gene symbols are auto-resolved to full names. Returns disease ORPHA codes, gene symbols, association types, and genomic locus information.

Quick Install

Run in Manus
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Installation

pip install tooluniverse

Status

Published

Reviewer

Automated import

Date Added

2026-03-30

Tags

tooluniverse orphanet rare-disease genetic-disorders